Inserm is a public scientific and technological institute which operates under the joint authority of the French Ministries of Health and Research. The institute is dedicated to biomedical research and human health, and is involved in the entire range of activities from the laboratory to the patient’s bedside. It also partners with the most prestigious research institutions in the world that are committed to scientific challenges and progress in these fields.
Researchers implicated in the project: Alexandra Tachtsidi, Giulia Scalisi and Laurie Lacombe
Genethon is a non-profit organization created in 1990 by the French association AFM-Telethon. Dedicated to the fight against rare diseases, Genethon has developed unique expertise in the design and development of gene therapy products, from laboratory research to clinical trials. Its work has resulted in several treatments on the market, in clinical trials, or at the R&D stage that are changing the lives of patients and their families. With its 200 scientists and professionals, Genethon pursues its mission: to develop treatments that change the lives of patients suffering from rare genetic diseases and to eradicate these pathologies