EDITSCD - Evaluation of genome-editing approaches for sickle cell disease

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Clinical genome editing to treat sikle cell disease – A brief update

P, Zarghamian, et al. « Clinical Genome Editing to Treat Sickle Cell Disease-A Brief Update ». Frontiers in Medicine, vol. 9, janvier [...]

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Base-Editing-Mediated Dissection of a γ-Globin Cis-Regulatory Element for the Therapeutic Reactivation of Fetal Hemoglobin Expression

Antoniou, Panagiotis, et al. « Base-Editing-Mediated Dissection of a γ-Globin Cis-Regulatory Element for the Therapeutic Reactivation of Fetal Hemoglobin Expression ». Nature Communications, [...]

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This project has received funding from the European Union’s Horizon Europe research and innovation programme under grant agreement No 101057659

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