Editing the Core Region in HPFH Deletions Alters Fetal and Adult Globin Expression for Treatment of β-Hemoglobinopathies

Venkatesan, Vigneshwaran, et al. « Editing the Core Region in HPFH Deletions Alters Fetal and Adult Globin Expression for Treatment of β-Hemoglobinopathies ». Molecular Therapy. Nucleic Acids, vol. 32, juin 2023, p. 671‑88. https://doi.org/10.1016/j.omtn.2023.04.024